A newly approved gene therapy cures blindness -- but it costs nearly $1M
When Elizabeth Guardino brought home her newborn from the hospital, he seemed a healthy, bright-eyed boy. But three months later, she realized something was amiss – Christian was unable to track objects placed in front of him and had developed no facial recognition.
Guardino knew something was horribly wrong and she needed to act quickly. He was diagnosed with a rare retinal disease called Leber congenital amaurosis, or LCA, and he spend nearly a decade in the dark.
“People born with this [mut